What are the responsibilities and job description for the Gene Editing Intern position at Sarepta Therapeutics, Inc.?
Why Sarepta? Why Now?
The promise of genetic medicine has arrived, and Sarepta is at the forefront. We hold leadership positions in Duchenne muscular dystrophy (DMD) and limb-girdle muscular dystrophies (LGMDs), and we currently have more than 40 programs in various stages of development in gene therapy, RNA and gene editing. In 2023, we launched our fourth therapy and the first ever gene therapy to treat Duchenne.
We’re looking for people who see unlimited potential in themselves and who are motivated by an unwavering commitment to patients.
What Sarepta Offers
At Sarepta, we care deeply about all the people in our community and believe in the importance of supporting them in all aspects of their lives. We aspire to maintain a culture that acknowledges people bring their whole selves to work, and we will strive to help everyone in our community integrate their work and personal lives while maintaining productivity.
The Importance of the Role
The Opportunity to Make a Difference
Develop 2D and 3D in vitro disease models.
Conduct experiments evaluating novel gene editing, RNA, and gene therapy strategies.
Maintain mammalian cell cultures and iPSC differentiations.
Perform molecular and cellular biology techniques: transfection, viral transduction, CRISPR-based gene editing, digital PCR, Western blot, cryosectioning, and IF.
Implement new methods and technologies for continuous improvement.
Troubleshoot routine technical challenges and contribute to their resolution in a timely manner.
Participate as part of a team in a laboratory setting contributing to a safe, efficient, and effective work environment.
Follow scientific direction to meet project timelines and deliverables.
Maintain compliant laboratory documentation and develop technical reports, protocols, and SOPs.
Interpret and present data to internal teams.
Perform other related duties as assigned.
More about You
Enrolled in a Master’s or PhD program in a scientific field with at least one year of relevant experience: neuromuscular disease, molecular biology, or genetic therapy research.
Hands-on experience with 2D/3D in vitro disease models and iPSC culture.
Proficiency in mammalian cell line engineering.
Skilled in molecular and cellular biology techniques: transfection, viral transduction, CRISPR-based gene editing, digital PCR, Western blot, cryosectioning, and IF.
Strong critical thinking and analytical skills.
Effective communication skills.
Ability to manage multiple projects and adapt to changing priorities.
Proficiency with Microsoft Office, GraphPad Prism, gene editing software, and other functional systems.
Passion for working in a dynamic, fast-paced team environment and making a difference in the lives of patients.
Join us and be part of a team that's transforming the future of genetic therapies!
Program Timeline:
This application is for a 12-week summer internship program that will start on May 19th and conclude on August 8th, 2025.
What Now?
We’re always looking for solution-oriented, critical thinkers.
So, if you’re comfortable with ambiguity and candor, relish challenging yourself, and place kindness and integrity at the forefront of how you approach your peers and work, then we encourage you to apply.
Salary : $21 - $25
